Gene therapy to treat Leber congenital amaurosis has recently shown some promise in revitalizing the gene therapy field.This is due in large part to injecting adeno- associated virus loaded with RPE65 just under the retina.What does the product of gene RPE65 do?
A) metabolizes retinal
B) metabolizes cone cell waste
C) metabolizes retinol
D) metabolizes rod cell waste
Correct Answer:
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