Gene therapy
A) has not yet been used successfully with mammals.
B) is a surgical technique that replaces defective genes with normal genes.
C) has been used successfully to treat victims of autosomal dominant disorders by replacing the dominant allele with a recessive allele.
D) is a genetic engineering technique that replaces defective alleles with normal ones.
E) is none of these.

Question

Quizplus · Accepted Answer

Gene therapy is a genetic engineering technique that involves replacing a defective allele with a normal one. It has been used successfully in clinical trials to treat genetic disorders such as severe combined immunodeficiency (also known as "bubble boy" disease) and hemophilia. While there are still significant challenges to overcome, gene therapy holds promise as a potential treatment for a wide range of genetic diseases.

Gene Therapy