Lipoprotein lipase deficiency is caused by a mutation in a single gene that codes for an enzyme (lipoprotein lipase) that is needed to break down fatty acids. A person who is homozygous recessive for this defective gene often suffers from severe pancreatitis, which can be deadly. A treatment that replaces this gene is __________.

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Gene therapy is a treatment that involves introducing a healthy copy of a gene into a patient's cells to replace a defective or missing gene, which in the case of lipoprotein lipase deficiency, would aim to provide a functional version of the lipoprotein lipase gene to correct the underlying genetic issue.

Lipoprotein Lipase Deficiency Is Caused by a Mutation in a Single