Cystic fibrosis (CF) is the most common inherited disease of Caucasians. It is due to mutations in an ABC transporter, the cystic fibrosis transmembrane conductance regulator (CFTR), which is a Cl^- and bicarbonate channel. Why have efforts at gene therapy to correct CF concentrated on the lungs when CF affects other tissues as well?

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The Answer of Cystic fibrosis (CF) is the most common inherited disease of Caucasians. It is due to mutations in an ABC transporter, the cystic fibrosis transmembrane conductance regulator (CFTR), which is a Cl^- and bicarbonate channel. Why have efforts at gene therapy to correct CF concentrated on the lungs when CF affects other tissues as well?

Cystic Fibrosis (CF) Is the Most Common Inherited Disease of Caucasians